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Duchenne muscular dystrophy (DMD) is caused by genetic changes that prevent the body from producing…
News
The Phase 3 SAPPHIRE study aims to assess the safety and effectiveness of apitegromab used in…
Blog
Facioscapulohumeral muscular dystrophy (FSHD) is the third most common inherited muscular dystrophy…
Your story
This year, we will be funding 12 exciting research projects, including three three-year project…
Blog
Myotonic dystrophy is a genetic condition that causes progressive muscle weakness and wasting. It…
News
As part of Spinal Muscular Atrophy Awareness Month, we split up our past SMA Muscles Matter videos…
News
Within Avalglucosidase alfa’s approval process, MDUK took part in a NICE Scoping Workshop in…
Blog
Through our research into better drugs and treatments, and our involvement in the NICE and the SMC…
News
We’re delighted to announce that a new treatment for Pompe disease has been recommended for use by…
News
We were joined by Neuromuscular Care Advisors Pam Appleton, from St Georges University Hospital,…