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On Monday 17 August, Roche announced that the European Medicines Agency (EMA) has validated the…
Your story
Chloe Smith, whose three-year-old son, Jenson, has a muscle-wasting condition, knows how difficult…
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The treatment, which could be the third for the condition, alongside Spinraza and Zolgensma, will…
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Today – on Changing Places Awareness Day – we are delighted to announce that changes will be made…
Blog
If you know me, you’ll know my favourite subject is TOILETS. Yes, toilets is a strange subject to…
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The first document, which answers questions about Spinraza and how it works, can be found here.…
News
Patients who are eligible under the terms set out in the Managed Access Agreement will be able to…
News
AveXis, which developed the treatment, announced the news on its website. You can read its press…
Press release
Many people living with muscle-wasting conditions are “clinically extremely vulnerable” and are…
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NICE, NHS England and NHS Improvement have reviewed the potential impact of COVID-19 on the…