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Acceleron Pharmaceuticals has announced preliminary results from its phase 2 trial testing ACE-083…
News
Summit Therapeutics has released interim results from their ongoing PhaseOut DMD study. The 48-week…
News
Today, the Committee for Medicinal Products for Human Use (CHMP) has returned a second negative…
News
A study from MDUK-funded researchers at University College London (UCL) and Royal Holloway…
News
Danish biotech company, Orphazyme, has assumed sponsorship of a phase 2/3 trial assessing the…
News
US scientists have created a new mouse model of Duchenne muscular dystrophy (DMD) and treated it…
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AveXis is expanding its spinal muscular atrophy (SMA) clinical development programme for its gene…
News
Lung function data from some of Sarepta’s Exondys 51 trials has been published in the Journal of…
Publication
You’ll find a snapshot of what the charity is funding in research, and how these research projects …
Publication
It gives a roundup of the latest news on research into muscle-wasting conditions as well as an…