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On Friday, 22 September, PTC Therapeutics, the company that manufactures Translarna, issued a…
News
Translarna currently has a conditional marketing approval (authorisation) from the EMA, given in…
Blog
I decided to get involved with fundraising for Muscular Dystrophy UK (MDUK) as my dad, Edward,…
Blog
“Today has definitely been one for the memory box.”
Louisa, whose son, Archie, lives with…
Blog
Running for Andrew
Graham recently decided to get back into running after a long break and last…
News
Our new research grants cover a variety of different muscle-wasting conditions, such as ADSSL1…
News
NICE recommendations
Although not NICE's final guidance on this medicine, the draft guidance…
Blog
Reducing inequalities
Tackling health inequalities is a long-standing aim of both the UK…
Publication
It is only through your help that we are able to fund vital research, and offer care and support to…
Your story
A swan is gracious and tough above water, but underneath she paddles 100 miles an hour – unseen. I…