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Catherine Woodhead, Chief Executive Officer at Muscular Dystrophy UK, said: Exondys 51 is not a…
Press release
The study is exciting as it used the technique to boost dystrophin production, key to combatting…
Press release
  A £35,000 investment into a rare genetic condition at St Andrews University will ‘bring hope’ to…
News
Researchers at University College London (UCL) have developed artificial ‘mini-muscles’ that could…
Press release
Spinraza is the first and only treatment for patients with the rare inherited muscle-wasting…
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Acceleron Pharma has announced the US Food and Drug Administration (FDA) has granted Fast Track…
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The 11th UK Neuromuscular Translational Research Conference was held in Cambridge on 19-20 April…
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Researchers in Scotland have found that a protein called neurochondrin may play a role in spinal…
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Summit Therapeutics has announced it has completed dosing participants in its Phase II PhaseOut DMD…
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Solid Biosciences has announced that the FDA has allowed the high-dose group to be included in the …